Project title:
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“Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer to Utilize Platelet-Derived Factor VIII for Hemophilia A” |
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Principal Investigator:
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David A. Wilcox, PhD, Medical College of Wisconsin |
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| Project title: |
“Lentiviral Vector for the Treatment of Fanconi Anemia” |
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| Principal Investigator: |
W. Scott Goebel, MD, PhD, Indiana University School of Medicine |
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| Co-Investigator: |
Grzegorz Nalepa, MD, PhD, Indiana University School of Medicine |
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| Project title: |
“Pulmonary Transplantation of Autologous CD34+ Cell Derived Macrophages for Hereditary Pul-monary Alveolar Proteinosis” |
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| Principal Investigator: |
Bruce Trapnell, MD, Cincinnati Children’s Hospital Medical Center |
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| Co-Investigator: |
Thomas Moritz, MD, Hanover Medical School |
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| Project title: |
Therapeutic BCL11A enhancer editing for the β-hemoglobin disorders |
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| Principal Investigator: |
Daniel E. Bauer, MD PhD, Boston Children’s Hospital, Harvard Medical School |
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| Project title: |
Clinical development of CAR T cell therapy targeting CD70 in glioblastoma |
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| Principal Investigator: |
Jianping Huang, MD, PhD, University of Florida |
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| Co-Investigator: |
Duane A. Mitchell, MD, PhD, University of Florida |
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| Project title: |
Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for Sickle Cell Disease |
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| Principal Investigator: |
Lakshmanan Krishnamurti, MD, Emory University |
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