Current supported projects


Project title:
“Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer to Utilize Platelet-Derived Factor VIII for Hemophilia A” Identifier:
Principal Investigator:
David A. Wilcox, PhD, Medical College of Wisconsin
Project title:  “Lentiviral Vector for the Treatment of Fanconi Anemia”
Principal Investigator: W. Scott Goebel, MD, PhD, Indiana University School of Medicine
Co-Investigator:  Grzegorz Nalepa, MD, PhD, Indiana University School of Medicine
Project title:  “Pulmonary Transplantation of Autologous CD34+ Cell Derived Macrophages for Hereditary Pul-monary Alveolar Proteinosis”
Principal Investigator: Bruce Trapnell, MD, Cincinnati Children’s Hospital Medical Center
Co-Investigator:  Thomas Moritz, MD, Hanover Medical School
Project title:  Therapeutic BCL11A enhancer editing for the β-hemoglobin disorders
Principal Investigator: Daniel E. Bauer, MD PhD, Boston Children’s Hospital, Harvard Medical School
Project title:  Clinical development of CAR T cell therapy targeting CD70 in glioblastoma
Principal Investigator: Jianping Huang, MD, PhD, University of Florida
Co-Investigator:  Duane A. Mitchell, MD, PhD, University of Florida
Project title:  Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for Sickle Cell Disease
Principal Investigator: Lakshmanan Krishnamurti, MD, Emory University
Project title:  Atrial painting of AdKCNH2-G628S for the prevention of post-operative atrial fibrillation
Principal Investigator: J. Kevin Donahue, MD, University of Massachusetts Medical School
Project title:  NK cell therapy for AML
Principal Investigator: David Wald, MD PhD, Case Western Reserve University and University Hospitals Cleveland Medical Center