Current supported projects
Project title: |
“Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer to Utilize Platelet-Derived Factor VIII for Hemophilia A” | |
ClinicalTrials.gov Identifier: |
NCT03818763 | |
Principal Investigator: |
David A. Wilcox, PhD, Medical College of Wisconsin | |
Project title: | “Lentiviral Vector for the Treatment of Fanconi Anemia” | |
Principal Investigator: | W. Scott Goebel, MD, PhD, Indiana University School of Medicine | |
Co-Investigator: | Grzegorz Nalepa, MD, PhD, Indiana University School of Medicine | |
Project title: | “Pulmonary Transplantation of Autologous CD34+ Cell Derived Macrophages for Hereditary Pul-monary Alveolar Proteinosis” | |
Principal Investigator: | Bruce Trapnell, MD, Cincinnati Children’s Hospital Medical Center | |
Co-Investigator: | Thomas Moritz, MD, Hanover Medical School | |
Project title: | Therapeutic BCL11A enhancer editing for the β-hemoglobin disorders | |
Principal Investigator: | Daniel E. Bauer, MD PhD, Boston Children’s Hospital, Harvard Medical School | |
Project title: | Clinical development of CAR T cell therapy targeting CD70 in glioblastoma | |
Principal Investigator: | Jianping Huang, MD, PhD, University of Florida | |
Co-Investigator: | Duane A. Mitchell, MD, PhD, University of Florida | |
Project title: | Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for Sickle Cell Disease | |
Principal Investigator: | Lakshmanan Krishnamurti, MD, Emory University | |
Project title: | Atrial painting of AdKCNH2-G628S for the prevention of post-operative atrial fibrillation | |
Principal Investigator: | J. Kevin Donahue, MD, University of Massachusetts Medical School | |
Project title: | NK cell therapy for AML | |
Principal Investigator: | David Wald, MD PhD, Case Western Reserve University and University Hospitals Cleveland Medical Center |